Comprehensive Care for Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) is a disease that affects the central nervous system. It damages the nerve cells that control how muscles work. As a result, muscles slowly weaken and waste away. SMA is a genetic disease, and you can only get it if you inherit the gene for it from both parents.
Specialists at the Northwestern Medicine Neuromuscular Program at Northwestern Memorial Hospital offer comprehensive care for people with SMA.
Northwestern Memorial Hospital continues to treat a growing number of patients who have different types of SMA, including types 3 and 4.
Nusinersen and onasemnogene abeparvovec-xioi are currently the only FDA-approved treatments for SMA. Nusinersen, which is the only medication approved for both children and adults with SMA, has been shown to halt the progression of disease. It may also help people regain some of the motor function lost due to SMA.